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Factor VIIIa (LongAte)

✓ Approved

PolyTherics Limited · F8 · 重组蛋白

什么是 Factor VIIIa?

Factor VIIIa 是一种重组蛋白,由PolyTherics Limited研发。该药已获批,用于治疗相关适应症,给药途径:Injectable (Others)、Intravenous (IV)、Subcutaneous Injection。

药物档案

商品名LongAte
公司PolyTherics Limited
药物类别重组蛋白, 细胞治疗
分子靶点F8
给药途径Injectable (Others), Intravenous (IV), Subcutaneous Injection
状态Approved

作用机制

分子靶点

Factor VIIIa 作用于 1 个分子靶点:

F8coagulation factor VIII (AHF, FVIII)
需要更深入的分析?Noah AI 可解释复杂机制并与同类药物比较。

治疗适应症

Factor VIIIa 针对 1 个适应症,涉及 1 个治疗领域。

治疗领域疾病/病症分期
Congenital, familial and genetic disordersFactor VIII deficiency✓ Approved

相关研究文献

PubMedFrontiers in immunology2026-09-10

STN-DBS exerts neuroprotection and anti-inflammatory effects in a Parkinson's disease rat model.

Yuan Ying Y, Liu Qidan Q, Liu Peng P, Guo Lili L et al.

Parkinson's disease (PD) is a progressive neurodegeneration disease characterized by dopaminergic (DA) neuron loss, with chronic neuroinflammation. Subthalamic nucleus deep brain stimulation (STN-DBS) is clinically effective for the relief of parkinsonism motor symptoms. Here, we used a homemade device to investigate the effect of STN-DBS on neuroprotection and chronic neuroinflammation in a unilateral 6-hydroxydopamine (6-OHDA)-induced PD rat model. Male Sprague-Dawley rats received 6-OHDA injections into the striatum, followed by ipsilateral STN electrode implantation and high-frequency stimulation. Motor function was assessed by open-field and apomorphine-induced rotation tests. DA neuron survival, glial phenotype changes, and nuclear factor (NF)-κB pathway activity in the nigrostriatal system were evaluated using Western blotting, immunofluorescence, and RT-qPCR. STN-DBS improved motor deficits and decreased the loss of tyrosine hydroxylase-positive neurons. It promoted astrocytes presented a neuroprotective phenotype and increased expression of brain-derived neurotrophic factor, and microglia mainly presented an anti-inflammatory M2 phenotype instead of a pro-inflammatory M1 phenotype. These effects may be associated with IκB-α stabilization, the suppression of NF-κB hyperactivation, and the consequent reduction in the release of downstream pro-inflammatory cytokines. Our findings highlight that our homemade device for STN-DBS is capable of inhibiting NF-κB, modulating glial phenotypes, mitigating neuroinflammation, and ultimately ameliorating parkinsonism deficits.

PMID 42718453
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PubMedRegenerative biomaterials2026-09-10

Synergistic effects of berberine and adipose stem cells in a silk fibroin-PEG hydrogel for diabetic wound healing via macrophage polarization modulation.

Hu Xiaohao X, Xu Jia J, Zhong Yanping Y, Zheng Weihao W et al.

Diabetic wound repair remains a considerable clinical challenge, largely due to the limited efficacy of current therapies. Herein, we engineered a novel silk fibroin (SF)-polyethylene glycol (PEG) hydrogel (SPB) incorporated with berberine (BBR) and adipose-derived stem cells (ASCs) to synergistically promote diabetic wound healing. By optimizing the physicochemical properties of SPB, we found that a 7:3 SF:PEG ratio provided an ideal balance of pore size (25.83 ± 3.94 μm), mechanical strength (32.33 ± 4.07 kPa) and sustained BBR release. In vitro, SPB significantly enhanced ASC paracrine function, promoting the production of vascular endothelial growth factor (VEGF), fibroblast growth factor 2 (FGF-2), stromal cell-derived factor 1 (SDF-1), platelet-derived growth factor-BB (PDGF-BB), and transforming growth factor beta (TGF-β). Accordingly, SF-based hydrogel system (SPBA) markedly stimulated fibroblast proliferation and migration and enhanced endothelial cell angiogenesis. Moreover, SPBA effectively modulated macrophage repolarization from the pro-inflammatory M1 to the anti-inflammatory M2 phenotype, thereby suppressing inflammation. In vivo, SPBA demonstrated remarkable therapeutic efficacy in diabetic rat full-thickness skin wounds, accelerating wound closure, promoting re-epithelialization, collagen deposition and neovascularization, while reducing local inflammation. These results highlight SPBA as a highly efficient and promising biomaterial strategy for diabetic wound treatment.

PMID 42719899
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PubMedNature communications2026-09-10

Inflammatory neuropathy in mouse and primate models of colorectal cancer.

Gaffney Caitlyn M CM, Casaril Angela M AM, Mahmud Iqbal I, Wei Bo B et al.

Colorectal cancer survivors are at increased risk of developing neurological issues, particularly peripheral neuropathy and chronic pain. Although pre-existing neuropathy is a risk factor for chronic pain, tumor-induced neuropathy has not been firmly established in pre-clinical models. Consistent with clinical observations, we show that mice with colorectal cancer develop peripheral neuropathy, which was associated with subtle locomotor deficits, without overt hypersensitivity. We detected widespread differences in pro-inflammatory cytokines and lipid metabolites in peripheral nerves from tumor-bearing mice. Macrophage accumulation, myelin decompaction and ryanodine receptor oxidation were associated with dysfunctional calcium homeostasis and reduced spike amplitude in sensory neurons. Similar alterations in plasma inflammatory mediators and lipid metabolites were associated with neuropathy and macrophage accumulation in peripheral nerves of rhesus macaques with colorectal cancer. These findings suggest colorectal cancer is causally linked to a subacute form of chronic inflammatory demyelinating polyneuropathy across species, which may represent an under-reported, yet important risk factor for neurological dysfunction in colorectal cancer survivors.

PMID 42716932
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PubMedJBRA assisted reproduction2026-09-10

Effects of repeated ovarian hyperstimulation on gut microbiota composition in a mouse model.

Cavalcante Marcelo Borges MB, Sampaio Olga Goiana Martins OGM, Santos Sacha Aubrey Alves Rodrigues SAAR, Santiago Léo L et al.

This study investigated whether repeated cycles of controlled ovarian hyperstimulation (COH) influ-ence the gut microbiota composition in female mice. Eight-week-old female Swiss mice (n=20; 10 per group) underwent ten weekly COH treatments with ex-ogenous gonadotropins or received saline injections as con-trols. One week after the final treatment, fecal samples were collected for gut microbiota profiling using 16S rRNA gene sequencing (V4 region amplification; primers 515F/806R) on the Illumina MiSeq platform. Sequencing data were pro-cessed in QIIME2 with DADA2 for denoising and Green-genes-based taxonomic assignment. Alpha-diversity (Shan-non, Simpson, observed OTUs, Faith's PD) and beta-diversity (Bray-Curtis, Jaccard, unweighted/weighted UniFrac) metrics were calculated. Differential taxonomic abundance and bio-marker analyses were performed using Random Forest and LEfSe. Statistical significance was set at p<0.05. No significant differences were observed between COH and control groups for alpha-diversity in-dices (all p>0.05) or beta-diversity distances (PERMANO-VA p>0.05). Relative abundances across major taxonomic levels were similar, although the Firmicutes:Bacteroidetes ratio was lower in COH-treated mice. Biomarker analyses identified Bacteroidales, Erysipelotrichaceae, and Parabac-teroides as enriched in the COH group, while Rikenellaceae and Odoribacter were more abundant in controls. Repeated COH did not significantly alter overall gut microbial diversity in mice under the conditions tested. However, specific taxonomic shifts and biomark-er signatures were detected, indicating associations-not causality-between COH exposure and changes in microbi-ota composition. Further studies are needed to determine the functional and physiological implications of these as-sociations.

PMID 42720314
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PubMedSmall (Weinheim an der Bergstrasse, Germany)2026-09-10

Bio-Inspired Calorimetric Flow Sensor With Hierarchical Microfluidic Design For Flow-Acoustic Fusion Sensing.

Cao Yudong Y, Ye Hong H, Gong Zheng Z, Zhou Weitai W et al.

High-sensitive flow and acoustic sensors with wide detection range are essential for the intelligence of underwater robotics. To tackle the challenge of limited detection range of flow sensors, here we present a bio-inspired calorimetric flow sensor (BioCFS) with hierarchical microfluidic design, mimicking the graded neuromast location of fish lateral line. The BioCFS achieves a high velocity resolution of 20 µm·s-1 and a wide dynamic range of 0-3 m·s-1. The high-sensitive and wide-range BioCFS enables the functions of yaw angle and velocity estimation, obstacle recognition, and vortex source localization. Moreover, the BioCFS can perceive low-frequency underwater acoustic signals, demonstrating a benchmark acoustic sensitivity of 1.31 V·Pa-1. By integrating flow-acoustic fusion perception with deep-learning models, the sensor achieves an accuracy of 99.6% in classifying 12 types of underwater scenarios. The excellent sensor performance and flow-acoustic fusion sensing function of the BioCFS offer significant potential for environmental perception and intelligent navigation in underwater robotics.

PMID 42717516
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PubMedBlood2026-09-10

Cuplike nuclei and bimodal CD34 expression in adult KMT2A-rearranged pro-B acute lymphoblastic leukemia.

Xu Zhaodong Z, Roland Kristine K

PMID 42720167
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